US FDA approves Ionis Pharma's therapy to treat rare brain disorder
- Posted on September 3, 2026
- By Bing News
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US FDA approves Ionis Pharma's therapy to treat rare brain disorder
Sept 3 (Reuters) - The U.S. FDA on Thursday approved Ionis Pharmaceuticals' therapy to treat a rare disease that affects the brain's white matter, making it the first treatment to get the nod for the genetic disorder. Ionis' drug zilganersen, branded as Zanvastro, can be used to treat adults and pediatric patients with Alexander disease, a neurological disorder caused by mutations in a gene that
