Ultragenyx sets $3.95 million price for rare disease gene therapy
- Posted on September 17, 2026
- By Bing News
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Ultragenyx sets $3.95 million price for rare disease gene therapy
By Sriparna Roy and Kamal Choudhury Sept 17 (Reuters) - Ultragenyx Pharmaceutical said on Thursday it has set a U.S. list price of $3.95 million for its newly approved gene therapy Fayuvi, launching one of the world's most expensive drugs as a one-time treatment for a rare, fatal childhood disease. The U.S. Food and Drug Administration approved Fayuvi for pediatric patients with Sanfilippo
