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Novartis reports positive data for neuromuscular disorder drug

  • Posted on June 11, 2026
  • By Bing News
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  • 1 min read
Novartis reports positive data for neuromuscular disorder drug
Novartis reports positive data for neuromuscular disorder drug

Novartis NVS announced positive data from the biomarker cohort of the FORTITUDE phase I/II study. The FORTITUDE phase I/II study is a randomized, double-blind, placebo-controlled study evaluating the safety, tolerability, pharmacokinetics, pharmacodynamics and exploratory efficacy of delpacibart braxlosiran (del-brax) in patients with facioscapulohumeral muscular dystrophy (FSHD). Del-brax is an investigational antibody oligonucleotide conjugate...
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Bing News

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